The Next Stage Of Drug Development: How Orphan Drugs Are Giving Drugmakers New Life
However, a growing number of drugmakers are looking for treatments because of the incentives being offered, potentially creating opportunities for investors who choose wisely. Q1 2022 hedge fund letters, conferences and more What Makes A Disease "Rare"?Numerous sources, including a study published in the Orphanet Journal of Rare Diseases, state that there are more than 7,000 rare diseases, and only 5% of them have an effective treatment. The authors of the study estimate that about 30 million Americans live with rare diseases, which amounts to about one out of every 10 Americans. Different age...